Serrano-Gonzalo, Irene; López-de-Frutos, Laura; Lahoz-Gil, Carlos; Delgado-Mateos, Francisco; Fernández-Galán, María-Ángeles; Morales-Conejo, Montserrat; Calle-Gordo, María-Victoria; Ibarretxe-Gerediaga, Daiana; Madinaveitia-Ochoa, Andres; Albarracin-Arraigosa, Antonio; Balanzat-Muñoz, José; Correcher-Medina, Patricia; García-Frade, Luis-Javier; Hernández-Rivas, Jesús-María; Labbadia, Francesca; López-Dupla, Jesús-Miguel; Lozano-Almela, María-Luisa; Mora-Castera, Elvira; Noya-Pereira, María-Soledad; Ruiz-Guinaldo, María-Ángeles; del-Mar-Tormo-Diaz, María; Vitoria-Miñana, Isidro; Arevalo-Vargas, Isidro; Andrade-Campos, Marcio; Giraldo, Pilar
(BMC, 2023-12-15)
BACKGROUND: The availability of multiple treatments for type 1 Gaucher disease increases the need for real-life studies to evaluate treatment efficacy and safety and provide clinicians with more information to choose the ...