Vázquez-Costa, Juan-F; Povedano, Mónica; Nascimiento-Osorio, Andres-E; Moreno-Escribano, Antonio; Kapetanovic-García, Solange; Domínguez, Raúl; Expósito, Jessica-M; González, Laura; Marco, Carla; Medina-Castillo, Julita; Muelas, Nuria; Natera-de-Benito, Daniel; Nungo-Garzon, Nancy-Carolina; Pitarch-Castellano, Inmaculada; Sevilla, Teresa; Hervas, David
(WILEY, 2022-11)
BACKGROUND AND PURPOSE: The aim was to assess the safety and efficacy of nusinersen in adult 5q spinal muscular atrophy (SMA) patients. METHODS: Patients older than 15 years and followed for at least 6 months with one motor ...